A Safety and Efficacy Study of Cryopreserved OTL-200 for Treatment of Metachromatic Leukodystrophy (MLD)

NCT03392987 · clinicaltrials.gov ↗

PHASE2

Phase

COMPLETED

Status

10

Enrollment

INDUSTRY

Sponsor class

Conditions

Lysosomal Storage Disease
Metachromatic Leukodystrophy

Interventions

GENETIC: OTL-200

Sponsor

Orchard Therapeutics

Collaborators

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