# Natural History Study of CEP290-Related Retinal Degeneration

> **NCT03396042** · — · COMPLETED · sponsor: **Editas Medicine, Inc.** · enrollment: 26 (actual)

## Conditions studied

- Blindness
- Leber Congenital Amaurosis 10
- Vision Disorders
- Eye Diseases
- Eye Diseases, Hereditary
- Eye Disorders Congenital
- Retinal Disease
- Retinal Degeneration

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT03396042
- **Lead sponsor:** Editas Medicine, Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2017-12-17
- **Primary completion:** 2022-05-06
- **Final completion:** 2022-05-06
- **Target enrollment:** 26 (ACTUAL)
- **Last updated:** 2022-05-19


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03396042

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03396042, "Natural History Study of CEP290-Related Retinal Degeneration". Retrieved via AI Analytics 2026-06-03 from https://api.ai-analytics.org/clinical/NCT03396042. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
