Pegtibatinase As an Enzyme Therapy for Patients with Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (COMPOSE)

NCT03406611 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

ACTIVE_NOT_RECRUITING

Status

32

Enrollment

INDUSTRY

Sponsor class

Conditions

Homocystinuria

Interventions

DRUG: Pegtibatinase
DRUG: Placebo

Sponsor

Travere Therapeutics, Inc.