A Study of Fitusiran (ALN-AT3SC) in Severe Hemophilia A and B Patients Without Inhibitors
NCT03417245
·
clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
120
Enrollment
INDUSTRY
Sponsor class
Conditions
Hemophilia A
Hemophilia B
Interventions
DRUG:
fitusiran
DRUG:
factor concentrates
Sponsor
Genzyme, a Sanofi Company