Long-Term Follow-up Study for Patients From AVXS-101-CL-101

NCT03421977 · clinicaltrials.gov ↗

ACTIVE_NOT_RECRUITING

Status

13

Enrollment

INDUSTRY

Sponsor class

Conditions

Spinal Muscular Atrophy 1

Interventions

BIOLOGICAL: Onasemnogene Abeparvovec-xioi

Sponsor

Novartis Gene Therapies