A Study to Assess the Safety and Tolerability of SOBI003 in Pediatric MPS IIIA Patients

NCT03423186 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

COMPLETED

Status

6

Enrollment

INDUSTRY

Sponsor class

Conditions

Sanfilippo Syndrome Type A (MPS IIIA)

Interventions

DRUG: SOBI003

Sponsor

Swedish Orphan Biovitrum