# Efficacy Study of Gene Therapy for The Treatment of Acute LHON Onset Within Three Months

> **NCT03428178** · NA · UNKNOWN · sponsor: **Bin Li** · enrollment: 120 (actual)

## Conditions studied

- Acute LHON
- Onset Within Three Months
- Onset Between 3 to 6 Months
- Onset Between 6 to 12 Months
- Onset Between 12 to 24 Months
- Onset Between 24 to 60 Months
- Onset Over 60 Months

## Interventions

- **DRUG:** rAAV2-ND4

## Key facts

- **NCT ID:** NCT03428178
- **Lead sponsor:** Bin Li
- **Sponsor class:** OTHER
- **Phase:** NA
- **Study type:** INTERVENTIONAL
- **Status:** UNKNOWN
- **Start date:** 2018-01-08
- **Primary completion:** 2018-12-06
- **Final completion:** 2020-12-30
- **Target enrollment:** 120 (ACTUAL)
- **Last updated:** 2020-07-29


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03428178

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03428178, "Efficacy Study of Gene Therapy for The Treatment of Acute LHON Onset Within Three Months". Retrieved via AI Analytics 2026-05-30 from https://api.ai-analytics.org/clinical/NCT03428178. Licensed CC0.

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