Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia A
NCT03432520
·
clinicaltrials.gov ↗
ACTIVE_NOT_RECRUITING
Status
29
Enrollment
INDUSTRY
Sponsor class
Conditions
Hemophilia A
Interventions
GENETIC:
SPK-8011
GENETIC:
SPK-8016
Sponsor
Spark Therapeutics, Inc.