# Study of IV VTS-270 for Infantile Liver Disease Associated With Niemann-Pick Disease, Type C

> **NCT03471143** · PHASE1,PHASE2 · COMPLETED · sponsor: **Washington University School of Medicine** · enrollment: 4 (actual)

## Conditions studied

- Niemann-Pick Disease, Type C

## Interventions

- **DRUG:** VTS-270

## Key facts

- **NCT ID:** NCT03471143
- **Lead sponsor:** Washington University School of Medicine
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2019-02-22
- **Primary completion:** 2024-10-04
- **Final completion:** 2024-10-04
- **Target enrollment:** 4 (ACTUAL)
- **Last updated:** 2026-01-05

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03471143

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03471143, "Study of IV VTS-270 for Infantile Liver Disease Associated With Niemann-Pick Disease, Type C". Retrieved via AI Analytics 2026-07-16 from https://api.ai-analytics.org/clinical/NCT03471143. Licensed CC0.

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