# Strimvelis Registry Study to Follow-up Patients With Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID)

> **NCT03478670** · — · ENROLLING_BY_INVITATION · sponsor: **Fondazione Telethon** · enrollment: 50 (estimated)

## Conditions studied

- Immunologic Deficiency Syndromes

## Interventions

- **GENETIC:** Strimvelis

## Key facts

- **NCT ID:** NCT03478670
- **Lead sponsor:** Fondazione Telethon
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** ENROLLING_BY_INVITATION
- **Start date:** 2017-05-05
- **Primary completion:** 2045-12-31
- **Final completion:** 2045-12-31
- **Target enrollment:** 50 (ESTIMATED)
- **Last updated:** 2026-05-18


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03478670

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03478670, "Strimvelis Registry Study to Follow-up Patients With Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID)". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT03478670. Licensed CC0.

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