Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged 12 to <18 Years)
NCT03500094
·
clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
22
Enrollment
INDUSTRY
Sponsor class
Conditions
Fabry Disease
Interventions
DRUG:
Migalastat HCl 150 mg
Sponsor
Amicus Therapeutics