Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantation
Conditions
- Bone Marrow Failure Syndrome
- Thalassemia
- Sickle Cell Disease
- Diamond Blackfan Anemia
- Acquired Neutropenia in Newborn
- Acquired Anemia Hemolytic
- Acquired Thrombocytopenia
- Hemophagocytic Lymphohistiocytoses
- Wiskott-Aldrich Syndrome
- Chronic Granulomatous Disease
- Common Variable Immunodeficiency
- X-linked Lymphoproliferative Disease
- Severe Combined Immunodeficiency
- Hurler Syndrome
- Mannosidosis
- Adrenoleukodystrophy
Interventions
- DRUG: Thiotepa--single daily dose
- DRUG: Thiotepa--escalated dose
Sponsor
University of Florida
Collaborators