Sialic Acid Supplementation in N-Acetylneuraminic Acid Synthase (NANS) Deficiency
NCT03545568
·
clinicaltrials.gov ↗
NA
Phase
COMPLETED
Status
10
Enrollment
OTHER
Sponsor class
Conditions
N-Acetylneuraminic Acid Storage Disease
Interventions
OTHER:
Neu5Ac supplementation
Sponsor
University of Lausanne
Collaborators
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