A Study Evaluating the Efficacy and Safety of AG-348 in Regularly Transfused Adult Participants With Pyruvate Kinase Deficiency (PKD)

NCT03559699 · clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
27
Enrollment
INDUSTRY
Sponsor class

Conditions

Interventions

Sponsor

Agios Pharmaceuticals, Inc.