CAMPSIITE™ RGX-121 Gene Therapy in Subjects With MPS II (Hunter Syndrome)
NCT03566043
·
clinicaltrials.gov ↗
PHASE2,PHASE3
Phase
ACTIVE_NOT_RECRUITING
Status
48
Enrollment
INDUSTRY
Sponsor class
Conditions
Mucopolysaccharidosis Type II (MPS II)
Interventions
GENETIC:
RGX-121
Sponsor
REGENXBIO Inc.