# Lentiviral Gene Therapy for X-linked Severe Combined Immunodeficiency

> **NCT03601286** · PHASE1 · RECRUITING · sponsor: **Great Ormond Street Hospital for Children NHS Foundation Trust** · enrollment: 5 (estimated)

## Conditions studied

- Severe Combined Immunodeficiency, X-Linked

## Interventions

- **DRUG:** Lentiviral vector transduced CD34+ cells

## Key facts

- **NCT ID:** NCT03601286
- **Lead sponsor:** Great Ormond Street Hospital for Children NHS Foundation Trust
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** RECRUITING
- **Start date:** 2018-12-21
- **Primary completion:** 2026-08
- **Final completion:** 2026-08
- **Target enrollment:** 5 (ESTIMATED)
- **Last updated:** 2023-10-12


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03601286

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03601286, "Lentiviral Gene Therapy for X-linked Severe Combined Immunodeficiency". Retrieved via AI Analytics 2026-05-27 from https://api.ai-analytics.org/clinical/NCT03601286. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*