Long-term Follow-up Study in Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)
ACTIVE_NOT_RECRUITING
Status
Conditions
- Inherited Retinal Dystrophy Due to RPE65 Mutations
Interventions
- BIOLOGICAL: AAV2-hRPE65v2
Sponsor
Spark Therapeutics, Inc.