# Mucopolysaccharidosis VII Disease Monitoring Program

> **NCT03604835** · — · RECRUITING · sponsor: **Ultragenyx Pharmaceutical Inc** · enrollment: 50 (estimated)

## Conditions studied

- Mucopolysaccharidosis VII
- MPS VII
- MPS 7
- Sly Syndrome

## Interventions

- **OTHER:** No Intervention

## Key facts

- **NCT ID:** NCT03604835
- **Lead sponsor:** Ultragenyx Pharmaceutical Inc
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** RECRUITING
- **Start date:** 2018-01-29
- **Primary completion:** 2033-05
- **Final completion:** 2033-05
- **Target enrollment:** 50 (ESTIMATED)
- **Last updated:** 2026-04-15


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03604835

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03604835, "Mucopolysaccharidosis VII Disease Monitoring Program". Retrieved via AI Analytics 2026-05-27 from https://api.ai-analytics.org/clinical/NCT03604835. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
