BPX-501 T Cells Infused Post Stem Cell Transplant in Pediatrics With Non-Malignant Disorders Ineligible for BPU004 Study
NO_LONGER_AVAILABLE
Status
Conditions
- Hurler Syndrome
- Inherited Metabolic Disorder
- Lysosomal Storage Disorder
- Metachromatic Leukodystrophy
- Inborn Errors of Metabolism
Interventions
- BIOLOGICAL: rivogenlecleucel
- DRUG: rimiducid
Sponsor
Bellicum Pharmaceuticals