# Spinraza in Adult Spinal Muscular Atrophy

> **NCT03709784** · — · ACTIVE_NOT_RECRUITING · sponsor: **Washington University School of Medicine** · enrollment: 148 (estimated)

## Conditions studied

- Spinal Muscular Atrophy
- Spinal Muscular Atrophy Type II
- Spinal Muscular Atrophy Type 3

## Interventions

- **DRUG:** Observational study to examine safety, tolerability, and effectiveness of SPINRAZA® prescribed as part of standard of care
- **OTHER:** One time survey

## Key facts

- **NCT ID:** NCT03709784
- **Lead sponsor:** Washington University School of Medicine
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** ACTIVE_NOT_RECRUITING
- **Start date:** 2018-08-16
- **Primary completion:** 2024-12-31
- **Final completion:** 2025-01-01
- **Target enrollment:** 148 (ESTIMATED)
- **Last updated:** 2024-11-20


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03709784

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03709784, "Spinraza in Adult Spinal Muscular Atrophy". Retrieved via AI Analytics 2026-05-31 from https://api.ai-analytics.org/clinical/NCT03709784. Licensed CC0.

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