# Smith-Lemli-Opitz Syndrome and Cholic Acid

> **NCT03720990** · PHASE1,PHASE2 · COMPLETED · sponsor: **University of Nebraska** · enrollment: 12 (actual)

## Conditions studied

- Smith-Lemli-Opitz Syndrome

## Interventions

- **DRUG:** Cholic Acid

## Key facts

- **NCT ID:** NCT03720990
- **Lead sponsor:** University of Nebraska
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2021-03-27
- **Primary completion:** 2022-08-30
- **Final completion:** 2023-09-30
- **Target enrollment:** 12 (ACTUAL)
- **Last updated:** 2024-04-30

## Collaborators

- [object Object]
- [object Object]
- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03720990

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03720990, "Smith-Lemli-Opitz Syndrome and Cholic Acid". Retrieved via AI Analytics 2026-07-17 from https://api.ai-analytics.org/clinical/NCT03720990. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
