Direct Lentiviral Injection Gene Therapy for MLD
NCT03725670
·
clinicaltrials.gov ↗
NA
Phase
RECRUITING
Status
10
Enrollment
OTHER
Sponsor class
Conditions
Metachromatic Leukodystrophy (MLD)
Interventions
GENETIC:
Intrathecal and intravenous LV gene therapy
Sponsor
Shenzhen Geno-Immune Medical Institute