# Use of Phenylbutyrate Therapy for Patients With Pyruvate Dehydrogenase Complex Deficiency.

> **NCT03734263** · PHASE2 · COMPLETED · sponsor: **Fondazione Telethon** · enrollment: 1 (actual)

## Conditions studied

- Pyruvate Dehydrogenase Complex Deficiency

## Interventions

- **DRUG:** sodium phenylbutyrate

## Key facts

- **NCT ID:** NCT03734263
- **Lead sponsor:** Fondazione Telethon
- **Sponsor class:** OTHER
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2018-10-01
- **Primary completion:** 2019-07-30
- **Final completion:** 2020-12-30
- **Target enrollment:** 1 (ACTUAL)
- **Last updated:** 2021-10-13


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03734263

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03734263, "Use of Phenylbutyrate Therapy for Patients With Pyruvate Dehydrogenase Complex Deficiency.". Retrieved via AI Analytics 2026-05-27 from https://api.ai-analytics.org/clinical/NCT03734263. Licensed CC0.

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