Long-term Safety and Efficacy Study of Fitusiran in Patients With Hemophilia A or B, With or Without Inhibitory Antibodies to Factor VIII or IX
NCT03754790
·
clinicaltrials.gov ↗
PHASE3
Phase
ACTIVE_NOT_RECRUITING
Status
281
Enrollment
INDUSTRY
Sponsor class
Conditions
Hemophilia
Interventions
DRUG:
Fitusiran
Sponsor
Genzyme, a Sanofi Company