HELIOS-A: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis)
Conditions
- Amyloidosis, Hereditary
- Transthyretin Amyloidosis
Interventions
- DRUG: Patisiran
- DRUG: Vutrisiran
Sponsor
Alnylam Pharmaceuticals