# N-Acetyl-L-Leucine for Niemann-Pick Disease, Type C (NPC)

> **NCT03759639** · PHASE2 · COMPLETED · sponsor: **IntraBio Inc** · enrollment: 33 (actual)

## Conditions studied

- Niemann-Pick Disease, Type C

## Interventions

- **DRUG:** IB1001

## Key facts

- **NCT ID:** NCT03759639
- **Lead sponsor:** IntraBio Inc
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2019-09-04
- **Primary completion:** 2022-11-07
- **Final completion:** 2022-11-07
- **Target enrollment:** 33 (ACTUAL)
- **Last updated:** 2023-11-28


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03759639

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03759639, "N-Acetyl-L-Leucine for Niemann-Pick Disease, Type C (NPC)". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT03759639. Licensed CC0.

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