A Randomized, Double-blind, Placebo-controlled Study of Delandistrogene Moxeparvovec (SRP-9001) for Duchenne Muscular Dystrophy (DMD)
Conditions
- Muscular Dystrophy, Duchenne
Interventions
- GENETIC: delandistrogene moxeparvovec
- GENETIC: placebo
Sponsor
Sarepta Therapeutics, Inc.