# Long-Term Follow-up Study of ADVM-043

> **NCT03804021** · — · COMPLETED · sponsor: **Adverum Biotechnologies, Inc.** · enrollment: 6 (actual)

## Conditions studied

- Alpha-1 Antitrypsin Deficiency

## Interventions

- **GENETIC:** No Intervention

## Key facts

- **NCT ID:** NCT03804021
- **Lead sponsor:** Adverum Biotechnologies, Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2018-12-27
- **Primary completion:** 2021-12-06
- **Final completion:** 2021-12-06
- **Target enrollment:** 6 (ACTUAL)
- **Last updated:** 2024-09-20


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03804021

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03804021, "Long-Term Follow-up Study of ADVM-043". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT03804021. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
