Gene Therapy Trial for Platelet Derived Factor VIII Production in Hemophilia A

NCT03818763 · clinicaltrials.gov ↗

PHASE1

Phase

ACTIVE_NOT_RECRUITING

Status

5

Enrollment

OTHER

Sponsor class

Conditions

Hemophilia A

Interventions

BIOLOGICAL: Auto CD34+PBSC, transduced with a lentiviral vector encoding the B domain deleted from of human coagulation factor VIII

Sponsor

Medical College of Wisconsin