# Effects of Miglustat Therapy on Infantile Type of Sandhoff and Taysachs Diseases (EMTISTD)

> **NCT03822013** · PHASE3 · TERMINATED · sponsor: **Tehran University of Medical Sciences** · enrollment: 30 (actual)

## Conditions studied

- GM2 Gangliosidosis
- Supportive Care

## Interventions

- **DRUG:** Miglustat

## Key facts

- **NCT ID:** NCT03822013
- **Lead sponsor:** Tehran University of Medical Sciences
- **Sponsor class:** OTHER
- **Phase:** PHASE3
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2019-01-14
- **Primary completion:** 2025-09-10
- **Final completion:** 2025-09-10
- **Target enrollment:** 30 (ACTUAL)
- **Why stopped:** The number of controls was insufficient compared to case.
- **Last updated:** 2025-09-17

## Collaborators

- [object Object]
- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03822013

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03822013, "Effects of Miglustat Therapy on Infantile Type of Sandhoff and Taysachs Diseases (EMTISTD)". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT03822013. Licensed CC0.

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