A Natural History Study of Aspartylglucosaminuria
NCT03853876
·
clinicaltrials.gov ↗
TERMINATED
Status
8
Enrollment
INDUSTRY
Sponsor class
Stopped
Discontinued AGU development program
Conditions
Aspartylglucosaminuria
Aspartylglucosamidase (AGA) Deficiency
Lysosomal Storage Diseases
Sponsor
Neurogene Inc.