# Expanded Access for ATB200/AT2221 for the Treatment of Pompe Disease

> **NCT03865836** · — · AVAILABLE · sponsor: **Amicus Therapeutics**

## Conditions studied

- Pompe Disease

## Interventions

- **BIOLOGICAL:** ATB200
- **DRUG:** AT2221

## Key facts

- **NCT ID:** NCT03865836
- **Lead sponsor:** Amicus Therapeutics
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** EXPANDED_ACCESS
- **Status:** AVAILABLE
- **Start date:** —
- **Primary completion:** —
- **Final completion:** —
- **Target enrollment:** — (—)
- **Last updated:** 2025-09-15


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03865836

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03865836, "Expanded Access for ATB200/AT2221 for the Treatment of Pompe Disease". Retrieved via AI Analytics 2026-06-25 from https://api.ai-analytics.org/clinical/NCT03865836. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*