Lead-in Study to Collect Prospective Efficacy and Safety Data of Current FVIII Prophylaxis Replacement Therapy in Adult Hemophilia A Participants
Conditions
- Blood Coagulation Disorder
- Blood Coagulation Disorders, Inherited
- Coagulation Protein Disorders
- Hemophilia A
- Genetic Diseases, Inborn
- Genetic Diseases, X-Linked
- Hematologic Diseases
- Hemorrhagic Disorders
- Factor VIII Deficiency
Interventions
- DRUG: Standard of Care FVIII Replacement therapy
Sponsor
Spark Therapeutics, Inc.