# Natural History and Functional Status Study of Patients With Lafora Disease

> **NCT03876522** · — · COMPLETED · sponsor: **Ionis Pharmaceuticals, Inc.** · enrollment: 33 (actual)

## Conditions studied

- Lafora Disease

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT03876522
- **Lead sponsor:** Ionis Pharmaceuticals, Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2019-01-09
- **Primary completion:** 2022-04-01
- **Final completion:** 2022-04-01
- **Target enrollment:** 33 (ACTUAL)
- **Last updated:** 2022-09-28


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03876522

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03876522, "Natural History and Functional Status Study of Patients With Lafora Disease". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT03876522. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
