Testing SIROLIMUS in Beta-thalassemia Transfusion Dependent Patients
NCT03877809
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
26
Enrollment
OTHER
Sponsor class
Conditions
Beta-Thalassemia
Interventions
DRUG:
Sirolimus 0.5 mg
Sponsor
Rare Partners srl Impresa Sociale
Collaborators
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