Neutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pompe Disease
Conditions
- Pompe Disease
- Pompe Disease (Late-onset)
- Glycogen Storage Disease Type 2
- LOPD
- Lysosomal Storage Diseases
- Acid Maltase Deficiency
Interventions
- DIAGNOSTIC_TEST: Neutralizing Antibody to SPK-3006 capsid
Sponsor
Spark Therapeutics, Inc.