A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Conditions
- Progressive Familial Intrahepatic Cholestasis (PFIC)
Interventions
- DRUG: Maralixibat
- OTHER: Placebo
Sponsor
Mirum Pharmaceuticals, Inc.