A Study of Lumasiran in Infants and Young Children With Primary Hyperoxaluria Type 1
NCT03905694
·
clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
18
Enrollment
INDUSTRY
Sponsor class
Conditions
Primary Hyperoxaluria
Primary Hyperoxaluria Type 1 (PH1)
Interventions
DRUG:
Lumasiran
Sponsor
Alnylam Pharmaceuticals