Ambroxol Therapy for Patients With Type 1 Gaucher Disease and Suboptimal Response to Enzyme Replacement Therapy

NCT03950050 · clinicaltrials.gov ↗

PHASE2

Phase

COMPLETED

Status

40

Enrollment

OTHER

Sponsor class

Conditions

Gaucher Disease, Type 1

Interventions

DRUG: Ambroxol

Sponsor

Shaare Zedek Medical Center