# Transcriptome and Metabolic Analyses of CHAPLE Disease

> **NCT03950804** · — · UNKNOWN · sponsor: **Marmara University** · enrollment: 60 (estimated)

## Conditions studied

- CD55 - Cluster of Differentiation Antigen 55 Deficiency
- Primary Intestinal Lymphangiectasis
- Protein-Losing Enteropathies
- Complement Regulatory Factor Defect

## Interventions

- **DRUG:** Eculizumab Injection

## Key facts

- **NCT ID:** NCT03950804
- **Lead sponsor:** Marmara University
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** UNKNOWN
- **Start date:** 2018-06-15
- **Primary completion:** 2019-09-15
- **Final completion:** 2020-06-15
- **Target enrollment:** 60 (ESTIMATED)
- **Last updated:** 2019-08-14

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03950804

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03950804, "Transcriptome and Metabolic Analyses of CHAPLE Disease". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT03950804. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
