Study of Long-Term Safety and Efficacy on Gene Therapy in Glycogen Storage Disease Type Ia

NCT03970278 · clinicaltrials.gov ↗

COMPLETED

Status

12

Enrollment

INDUSTRY

Sponsor class

Conditions

Glycogen Storage Disease Type IA
Von Gierke's Disease (GSD Type Ia)

Interventions

OTHER: No intervention

Sponsor

Ultragenyx Pharmaceutical Inc