A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON)
NCT03992430
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clinicaltrials.gov ↗
PHASE3
Phase
ACTIVE_NOT_RECRUITING
Status
160
Enrollment
INDUSTRY
Sponsor class
Conditions
Muscular Dystrophy, Duchenne
Interventions
DRUG:
Eteplirsen
Sponsor
Sarepta Therapeutics, Inc.