# Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients

> **NCT04041102** · — · COMPLETED · sponsor: **University of Pennsylvania** · enrollment: 31 (actual)

## Conditions studied

- GM1 Gangliosidosis

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT04041102
- **Lead sponsor:** University of Pennsylvania
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2020-06-12
- **Primary completion:** 2024-05-01
- **Final completion:** 2024-05-01
- **Target enrollment:** 31 (ACTUAL)
- **Last updated:** 2025-10-24

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04041102

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04041102, "Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients". Retrieved via AI Analytics 2026-05-27 from https://api.ai-analytics.org/clinical/NCT04041102. Licensed CC0.

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