An Observational LTFU Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for ADA-SCID

Conditions

• Adenosine Deaminase Deficiency
• Severe Combined Immunodeficiency (SCID)

Interventions

• BIOLOGICAL: autologous ex vivo gene therapy products based on the EFS LV encoding for the human adenosine deaminase (ADA) gene (EFS-ADA LV)

Sponsor

University of California, Los Angeles

Collaborators

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