Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A
NCT04069533
·
clinicaltrials.gov ↗
PHASE2
Phase
ACTIVE_NOT_RECRUITING
Status
7
Enrollment
INDUSTRY
Sponsor class
Conditions
Fanconi Anemia Complementation Group A
Interventions
BIOLOGICAL:
RP-L102
Sponsor
Rocket Pharmaceuticals Inc.