Longitudinal Assessment of Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency Patients
ACTIVE_NOT_RECRUITING
Status
Conditions
- Neuronal Ceroid-Lipofuscinoses
- Neuronal Ceroid Lipofuscinosis CLN2
- Spinocerebellar Ataxia, Autosomal Recessive 7
Sponsor
Children's Hospital of Orange County