A Prospective and Retrospective Cohort Study in Patients With Chronic Forms of Acid Sphingomyelinase Deficiency (ASMD)
NCT04106544
·
clinicaltrials.gov ↗
NA
Phase
COMPLETED
Status
84
Enrollment
INDUSTRY
Sponsor class
Conditions
Sphingomyelin Lipidosis
Interventions
PROCEDURE:
Investigational Procedures
Sponsor
Sanofi