# A Prospective and Retrospective Cohort Study in Patients With Chronic Forms of Acid Sphingomyelinase Deficiency (ASMD)

> **NCT04106544** · NA · COMPLETED · sponsor: **Sanofi** · enrollment: 84 (actual)

## Conditions studied

- Sphingomyelin Lipidosis

## Interventions

- **PROCEDURE:** Investigational Procedures

## Key facts

- **NCT ID:** NCT04106544
- **Lead sponsor:** Sanofi
- **Sponsor class:** INDUSTRY
- **Phase:** NA
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2019-09-27
- **Primary completion:** 2023-05-15
- **Final completion:** 2023-05-15
- **Target enrollment:** 84 (ACTUAL)
- **Last updated:** 2023-08-16


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04106544

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04106544, "A Prospective and Retrospective Cohort Study in Patients With Chronic Forms of Acid Sphingomyelinase Deficiency (ASMD)". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT04106544. Licensed CC0.

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