Safety and Proof-of-Concept (POC) Study With AMT-130 in Adults With Early Manifest Huntington's Disease

NCT04120493 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

ACTIVE_NOT_RECRUITING

Status

43

Enrollment

INDUSTRY

Sponsor class

Conditions

Huntington's Disease

Interventions

GENETIC: intra-striatal rAAV5-miHTT
OTHER: Imitation (sham) surgery

Sponsor

UniQure Biopharma B.V.