# Gene Therapy for Chinese Hemophilia B

> **NCT04135300** · NA · COMPLETED · sponsor: **Institute of Hematology & Blood Diseases Hospital, China** · enrollment: 10 (actual)

## Conditions studied

- Hemophilia B

## Interventions

- **GENETIC:** Single dose intravenous injection of BBM-H901

## Key facts

- **NCT ID:** NCT04135300
- **Lead sponsor:** Institute of Hematology & Blood Diseases Hospital, China
- **Sponsor class:** OTHER
- **Phase:** NA
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2019-10-16
- **Primary completion:** 2022-01-07
- **Final completion:** 2022-01-07
- **Target enrollment:** 10 (ACTUAL)
- **Last updated:** 2025-02-21

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04135300

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04135300, "Gene Therapy for Chinese Hemophilia B". Retrieved via AI Analytics 2026-06-12 from https://api.ai-analytics.org/clinical/NCT04135300. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
